What are Advanced Therapies

Advanced Therapies is the collective term for a novel class of biological medicines that are based on genes, cells or tissue.

They offer ground-breaking opportunities for the treatment of disease and injury with the potential to improve clinical outcomes across a range of disease indications, including rare diseases where there are currently no or limited treatment options available.

Gene Therapies

involve the transfer of genetic material into the cells of a patient’s body to treat the underlying cause of a specific disease. This may involve genome editing technology to alter the patient’s DNA.

Somatic Cell Therapies

involve the transfer of intact, live cells into a patient to help lessen or cure a disease. The cells may originate from the patient’s own cells (autologous) or from a donor (allogenic).

Tissue Engineered Products

involve regenerating, replacing or repairing human cells, tissues or organs to restore or establish normal function. Current examples of these therapies use the patient’s own cells (autologous) for therapy manufacture.

Combined ATMP

involve cells or tissues that have been combined with one or more medical device(s).