# Advanced Therapies Wales ## Posts - [New NHS Readiness Toolkit Content](https://advancedtherapieswales.co.uk/new-nhs-readiness-toolkit-content/): Guidance to establish a shared care Advanced Therapy Medicinal Product (ATMP) trial within or across NHS Trusts/Health Boards The ATTC network has recently released a new resource: ‘Guidance to establish shared care Advanced Therapy Medicinal Product (ATMP) trials within or across NHS Trusts/Health Boards’ to support accelerated clinical trial set up through effective collaboration between disciplines/specialities within or across NHS Trusts/Health Boards, who are working under the same ATMP trial protocol.  The document is housed within our NHS Readiness Toolkit. As a guidance document, it can be located within the ‘National Infrastructure, templates and guidance’ section of the Clinical Trials area in this toolkit.   Please follow this link to… - [Flying the flag for Wales at Festival of Genomics!](https://advancedtherapieswales.co.uk/flying-the-flag-for-wales/): Last week, we attended the Festival of Genomics and Biodata at ExCeL London, where we were proud to support the many Welsh speakers and panel participants from across our own and partner organisations. Now in its 11th year, the festival featured an Advanced Therapies stage for the first time, providing an excellent platform to showcase the progress and impact of our work to date. It was fantastic to welcome so many people to our stand, eager to learn more about advanced therapies and our programme. The conversations were thoughtful, insightful and energising—it was a pleasure to meet you all. We… - [First Welsh patient receives advanced therapy to treat Haemophilia](https://advancedtherapieswales.co.uk/first-welsh-patient-receives-advanced-therapy-to-treat-haemophilia/): This week Cardiff and Vale University Health Board became the first facility in Wales to administer a revolutionary gene therapy to a patient with haemophilia. This milestone marks a major breakthrough in the treatment of haemophilia, offering new hope for patients living with this lifelong condition. Haemophilia, which is more common in men, is a rare inherited bleeding disorder which stops a person’s blood from clotting properly due to a lack of a protein known as ‘clotting factor’. There are two types: Haemophilia A, which affects approximately 1 in 5,000 males and Haemophilia B, which affects 1 in 30,000 males.… - [The power of patient voice](https://advancedtherapieswales.co.uk/the-power-of-patient-voice/): We recently attended the Advanced Therapies Integrates event at Victoria House London. A key theme throughout the discussions on the day, was the importance of community and collaboration. Advanced therapies rely not only on strong science, but also on the partnerships and people behind them. We were delighted to be asked to join a panel discussion entitled “In Their Shoes” highlighting real, lived experience from patients and their families, discussing why the patient perspective is so important. CAR-T therapy patient, Sandra Leadley-Watkins shared her story following her lymphoma diagnosis. After exhausting various treatment options, Sandra was offered CAR-T therapy, and has been in remission since receiving… - [Pioneering virus technology for solid tumours](https://advancedtherapieswales.co.uk/pioneering-virus-technology-for-solid-tumours/): The first patient has been treated in a clinical trial that is testing a pioneering virus technology – which originated at Cardiff University – that infects cancer cells, producing an anti-tumour drug from inside the tumour cells. Accession Therapeutics’ ATTEST trial is a first-in-human Phase 1 trial in solid tumour patients, testing TROCEPT-01 (also known as ATTR-01). The trial is being delivered by Velindre University NHS Trust and Cardiff and Vale University Health Board. The ATTEST trial is recruiting into leading UK clinical sites – including Cardiff – with plans to extend to Spain. Professor Adel Samson at Leeds University… - [Cardiff's leading health partners unite](https://advancedtherapieswales.co.uk/cardiffs-leading-health-partners-unite/): Cardiff Health Partners is a unique collaboration between three of Cardiff’s leading health organisations to strengthen healthcare delivery, foster research excellence, economic growth, and social wellbeing across the capital and wider South East Wales region. As its interim Managing Director, Mrs Savery will operate across the strategic partnership with overall responsibility for ensuring the transformative potential of CHP is on track to be delivered. “I’m delighted to take on this role at such an exciting time for Cardiff Health Partners. This collaboration brings together world-class expertise to improve patient care, accelerate research, and create real economic and social benefits for… - [The first UK Advanced Therapies Clinical Expertise Forum](https://advancedtherapieswales.co.uk/a-uk-first-for-advanced-therapies-wales/): The Advanced Therapies Wales Clinical Expertise Forum, the UK’s first model of its kind for Advanced Therapies, was endorsed by ATW Programme Board in December 2024 to embed multidisciplinary clinical leadership within the Advanced Therapies Wales programme. Its remit includes service design, workforce planning, business case development, and infrastructure preparation, ensuring alignment with regulatory standards such as the Medicines and Healthcare products Regulatory Agency (MHRA), the Joint Accreditation Committee ISCT-Europe & EBMT (JACIE), and the Innovative Licensing and Access Pathway (ILAP) across Wales. Speciality Leads roles have been identified for the following areas, to be funded by the ATW Programme… - [Third ATW National Symposium](https://advancedtherapieswales.co.uk/third-atw-national-symposium/): Launched in 2023 as a small stakeholder event, The Advanced Therapies Wales Symposium has matured into a flagship annual gathering for clinicians, researchers, industry, patients, and policymakers. The 2025 event saw an almost two-fold increase in delegate registrations, highlighting its expanding reach and influence. The theme of patient and public involvement and engagement took centre stage this year and included a patient speaker as part of a jam-packed agenda. The morning was broken down into fast paced flash talk sessions, covering the research environment as well as standard care, including a patient talking about their own experience. In the afternoon… - [New trial for gene therapy for frontotemporal dementia](https://advancedtherapieswales.co.uk/new-trial-for-gene-therapy-for-frontotemporal-dementia/): A new clinical trial, delivered in Cardiff, will investigate the use of a one-time gene therapy to stop the disease progression in patients with frontotemporal dementia. The trial, run by AviadoBio, will recruit patients from across Europe. The Advanced Neurotherapies Centre at Cardiff University and Cardiff and Vale University Health Board will be the UK surgical site for the trial, as the centre is the only place in the UK that can deliver drugs straight to the human brain in an MRI scanner for precise treatment and real-time imaging. The goal of this clinical study is to learn about an… ## Pages - [404 - Page Not Found](https://advancedtherapieswales.co.uk/404-page-not-found/) - [Training](https://advancedtherapieswales.co.uk/resources/training/) - [Toolkits](https://advancedtherapieswales.co.uk/resources/toolkits/) - [Horizon Scanning](https://advancedtherapieswales.co.uk/resources/horizon-scanning/) - [Glossary](https://advancedtherapieswales.co.uk/resources/glossary/) - [Resources](https://advancedtherapieswales.co.uk/resources/) - [Funding](https://advancedtherapieswales.co.uk/resources/funding/) - [Multi-Disciplinary Research Group](https://advancedtherapieswales.co.uk/about-us/multi-disciplinary-research-group-mdrg/) - [Our Partners](https://advancedtherapieswales.co.uk/about-us/our-partners/) - [About us](https://advancedtherapieswales.co.uk/about-us/) - [Accessibility](https://advancedtherapieswales.co.uk/accessibility/) - [Cookies](https://advancedtherapieswales.co.uk/cookies/) - [Privacy](https://advancedtherapieswales.co.uk/privacy/) - [Patient & Public Involvement and Engagement](https://advancedtherapieswales.co.uk/patient-public-involvementand-engagement/) - [Available therapies](https://advancedtherapieswales.co.uk/available-therapies/) - [Statement of Intent](https://advancedtherapieswales.co.uk/about-us/statement-of-intent/) - [Delivery Plan](https://advancedtherapieswales.co.uk/about-us/delivery-plan/) - [Events](https://advancedtherapieswales.co.uk/events/) - [News](https://advancedtherapieswales.co.uk/news/) - [Home](https://advancedtherapieswales.co.uk/) ## Optional - [Agent (MCP protocol)](websites-agents.hostinger.com/advancedtherapieswales.co.uk/mcp) [comment]: # (Generated by Hostinger Tools Plugin)